FDA grants accelerated approval of tofersen for treatment of SOD1-ALS
The Food and Drug Administration granted accelerated approval of the drug tofersen for the treatment of SOD1-ALS. Developed by…
Research Byte: Packard researchers identify new function of C9 protein
In a new paper in PLOS Genetics, Packard researcher Jiou Wang identified a new mechanism through which C9orf72…
Answer ALS is proud to announce the public release of new in-depth biological and clinical datasets to aid ALS research
A new set of Answer ALS project data is now available through the Answer ALS Data Portal. A…
New links between toxic protein and ALS discovered
Neuroscientists at Thomas Jefferson University have identified a new way that repeat expansion in the C9orf72 gene—the most…
New Phase 2 trial results show promise for ALS
Results of a new Phase 2 randomized clinical trial in 137 patients with ALS showed that treatment with…
Key link uncovered between C9orf72 mutation and TDP-43 pathology in ALS/FTD
In a new study, a team of Packard scientists identified a key intersection between two major pathways of…
Legacy of Terror and Hope
For people with inherited forms of ALS, learning of their genetic predisposition can feel like a “death sentence.”…
Answer ALS Launches ‘The Data is Here’ Campaign to Announce the Release of the World’s Largest Open-Sourced ALS Data Portal
Answer ALS Launches ‘The Data is Here’ Campaign to Announce the Release of the World’ Largest Open-Sourced ALS…
Answer ALS Partners to Launch the ‘End ALS Challenge’ Digital Competition
Administered by Kaggle, the End ALS Challenge asks participants to help identify solutions to the disease NEW ORLEANS,…
Packard scientists have identified a new mechanism by which mutations in the UBQLN2 gene lead to ALS
Teams from the University of Maryland and Harvard University have showed that ALS-linked mutations in UBQLN2 compromise import…