FDA grants accelerated approval of tofersen for treatment of SOD1-ALS
The Food and Drug Administration granted accelerated approval of the drug tofersen for the treatment of SOD1-ALS. Developed by…
Breaking Research
Research Byte: Packard researchers identify new function of C9 protein
In a new paper in PLOS Genetics, Packard researcher Jiou Wang identified a new mechanism through which C9orf72…
Answer ALS Launches ‘The Data is Here’ Campaign to Announce the Release of the World’s Largest Open-Sourced ALS Data Portal
Answer ALS Launches ‘The Data is Here’ Campaign to Announce the Release of the World’ Largest Open-Sourced ALS…
ALS Pathology Linked to Defects in the Cell Nucleus
Packard researchers used Answer ALS cell lines to show that the protein CHMP7 accumulates in the nucleus, triggering…
The Pathway to Discovery and Hope for ALS Patients and Researchers: A massive biological genetic and clinical resource for ALS and neurodegenerative diseases.
Every year, 5,000 Americans are diagnosed with amyotrophic lateral sclerosis (ALS), also known as Lou Gehrig’s disease, that…